A small but provocative study showed that a form of gene therapy significantly improved the vision of patients left legally blind by a rare genetic eye disease. The benefit was especially striking among children. Researchers said the findings amount to an important advance toward medicine's ambitious but generally unrealized dream of replacing disease-causing mutant or missing genes with normal DNA to treat and cure debilitating illnesses In the study, 12 patients, including four children between ages 8 and 11 years old, underwent a surgical procedure in which a gene that makes a protein critical to vision function was injected into one eye
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Study shows hope for type of blindness
